(RTTNews) - Ultragenyx Pharmaceutical Inc. (RARE) on Thursday said the U.S. Food and Drug Administration has accepted its resubmitted Biologics License Application seeking accelerated approval for UX111, an AAV9 gene therapy for the treatment of Sanfilippo syndrome Type A.
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Ultragenyx BLA For UX111 Gene Therapy Accepted By FDA
(RTTNews) - Ultragenyx Pharmaceutical Inc. (RARE) on Thursday said the U.S. Food and Drug Administration has accepted its resubmitted Biologics License Application seeking accelerated approval for UX111, an AAV9 gene…
